High dose TSHA-102 was generally well tolerated with no SAEs or DLTs in two adolescent/adult patients and one <a target=_blank href= ...

Presented positive interim data for 4D-150 in wet age-related macular degeneration (wet AMD) from PRISM Phase 1/2 clinical trial highlighting ...

NGN-401 uses an adeno-associated virus serotype 9 vector to deliver a full-length functional MECP2 gene using the firm's EXACT transgene regulation technology. NGN-401 is under evaluation in the FDA's ...

AAV is the top vector choice for use in gene therapies for its stable expression, strong biosafety rating, low immunogenicity, convenient ocular delivery routes and high product stability. Dr. Lu will ...

Diamond-Blackfan anemia (DBA) is a potentially life-threatening condition that can cause severe anemia and other abnormalities. It's a rare genetic blood disorder that occurs when the bone marrow ...

This clinical-grade vector is ready, and the team hopes to take it to clinical trial next.Vijay Sankaran, MD, PhD, lead and corresponding author of the paper, is available for comment if you’re ...

Senior officials from the US Navy and Japan Maritime Self-Defense Force joined the crew of the JS Kaga, as F-35B pilots from ...

TD Cowen analyst Tyler Van Buren has maintained their bullish stance on RCKT stock, giving a Buy rating today. Tyler Van Buren has given his ...

As previously announced, IMUNON plans to hold an End-of-Phase 2 meeting with the U.S. Food and Drug Administration (FDA) in person to discuss the design for a Phase 3 pivotal study of IMNN-001 in ...

ProBioGen’s AGE1.CR.PIX been developed as a stable proliferating avian cell line that is highly permissive for different ...