Learn about the groundbreaking gene therapy for sickle cell disease at Manning Family Children's Hospital in Louisiana, ...
Agios (AGIO) downgraded to Hold as Novo Nordisk rivalry and FDA/REMS risks hit sickle cell & thalassemia; pipeline and cash ...
Despite data gaps in many countries, the burden of sickle cell disease, especially in west and central Africa, underscores ...
If the Sickle Cell Disease Protection Act is signed into law by Governor Kemp, the Act would mandate the Georgia Department ...
A new study shows Nigeria has the world's highest burden of sickle cell disease in children, with over 1.5 million affected.
The government has launched the KETAN project, marking a critical step in addressing sickle cell disease, a major public ...
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$3 million prize goes to duo whose research led to first sickle cell CRISPR therapy
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
Etavopivat showed a 27% reduction in vaso-occlusive crisis events and ~4-month delay to first vaso-occlusive crisis event on ...
On Tuesday, the first person in the state to receive gene therapy for sickle cell disease left the hospital after a ...
Novo Nordisk acquired rights to etavopivat when it bought Forma Therapeutics for $1.1 billion in 2022, when the drug was in ...
Negative descriptors were present in 15% of notes for sickle cell patients; 14% of notes for patients with opioid use ...
Topline data for the once-daily PKR activator etavopivat demonstrate a 27% reduction in vaso-occlusive crises and a robust hematologic response in patients with SCD.
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