Austin Louis, 20, says the CRISPR treatment he received at the Children's Hospital of Philadelphia for sickle cell disease ...

Louis was the first patient at Children's Hospital of Philadelphia — outside of a clinical trial — to get a new FDA-approved treatment. It involves collecting his stem cells, which are then ...

A new breakthrough study led by researchers at the University of Minnesota Twin Cities could explain why patients with the ...

Black History Month is poignant for one family after a man got a historic, innovative treatment at Children's Hospital of Philadelphia.

The Director of the National Centre of Excellence for Sickle Cell Disease Research and Training, Prof. Obiageli Nnodu, said early screening and continuous care significantly reduce under-five ...

Zydus Lifesciences on Friday said the U.S. health regulator has granted Orphan Drug Designation to Desidustat, a novel oral ...

Vertex executives warned that Casgevy, its curative treatment for sickle cell disease, would be slow to reach patients. But ...

James Griffin, diagnosed with sickle cell at age two, shares how blood donations enabled his transformation from frequent hospital patient to medical professional and advocate.

Malcolm survived a brain aneurysm in 2019 and credited the surgeon with saving his life. The doctor’s expertise in sickle ...

A spotlight is being focused this weekend on a debilitating disease, that health experts say needs greater awareness. It's ...

Zydus Lifesciences announced a significant development today. The US Food and Drugs Administration has granted Orphan Drug ...