Agios (AGIO) downgraded to Hold as Novo Nordisk rivalry and FDA/REMS risks hit sickle cell & thalassemia; pipeline and cash ...
Despite data gaps in many countries, the burden of sickle cell disease, especially in west and central Africa, underscores ...
If the Sickle Cell Disease Protection Act is signed into law by Governor Kemp, the Act would mandate the Georgia Department ...
On Tuesday, the first person in the state to receive gene therapy for sickle cell disease left the hospital after a ...
Etavopivat showed a 27% reduction in vaso-occlusive crisis events and ~4-month delay to first vaso-occlusive crisis event on ...
In season 1, episode 2 of the popular show "The Pitt," a Black woman with sickle cell disease arrives at the emergency ...
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
Topline data for the once-daily PKR activator etavopivat demonstrate a 27% reduction in vaso-occlusive crises and a robust hematologic response in patients with SCD.
Key takeawaysResults from a UCLA-led clinical trial for sickle cell disease reveal the unique challenges of treating blood disorders with gene therapy ...
Novo Nordisk acquired rights to etavopivat when it bought Forma Therapeutics for $1.1 billion in 2022, when the drug was in ...
A landmark international study has revealed a sobering public health milestone: Nigeria now carries the highest burden of ...
The government has launched the KETAN project, marking a critical step in addressing sickle cell disease, a major public ...
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