Two papers published in The New England Journal of Medicine highlight the potential of gene editing for treatment of sickle ...
Learn about the groundbreaking gene therapy for sickle cell disease at Manning Family Children's Hospital in Louisiana, ...
Tessera Therapeutics (“Tessera”), the biotechnology company pioneering a new approach in genetic medicine known as Gene Writing™, today announced four presentations of new preclinical data at the ...
Agios (AGIO) downgraded to Hold as Novo Nordisk rivalry and FDA/REMS risks hit sickle cell & thalassemia; pipeline and cash ...
Despite data gaps in many countries, the burden of sickle cell disease, especially in west and central Africa, underscores ...
If the Sickle Cell Disease Protection Act is signed into law by Governor Kemp, the Act would mandate the Georgia Department ...
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$3 million prize goes to duo whose research led to first sickle cell CRISPR therapy
Dr. Swee Lay Thein and Dr. Stuart Orkin won the $3 million Breakthrough Prize in Life Sciences for their work toward a ...
A new study shows Nigeria has the world's highest burden of sickle cell disease in children, with over 1.5 million affected.
Etavopivat showed a 27% reduction in vaso-occlusive crisis events and ~4-month delay to first vaso-occlusive crisis event on ...
Novo Nordisk acquired rights to etavopivat when it bought Forma Therapeutics for $1.1 billion in 2022, when the drug was in ...
On Tuesday, the first person in the state to receive gene therapy for sickle cell disease left the hospital after a ...
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