The American Journal of Managed Care

Review Examines Interstitial Lung Disease in Lysosomal Storage Disorders

This new analysis shows early diagnosis of some lysosomal storage disorders can help avoid irreversible damage across the board. Lysosomal storage disorders (LSDs), including Gaucher disease (GD), ...
Yahoo Finance

Lysosomal Storage Disease Treatment Market Analysis Report 2025-2034: Breakthroughs in Enzyme & Gene Therapies, Early Diagnosis Drive Demand

Dublin, Sept. 17, 2025 (GLOBE NEWSWIRE) -- The "Lysosomal Storage Disease Treatment Market Opportunity, Growth Drivers, Industry Trend Analysis, and Forecast 2025-2034" report has been added to ...
Business Wire

M6P Therapeutics Presents Promising Preclinical Data in Lysosomal Storage Disorders at the 17 th Annual WORLDSymposium™ 2021

ST. LOUIS--(BUSINESS WIRE)--M6P Therapeutics, a privately held life sciences company developing next-generation recombinant enzyme and gene therapies for lysosomal storage disorders (LSDs), announced ...
Odessa American

M6P Therapeutics Receives Six Rare Pediatric Disease Designations from the U.S. FDA for Company’s Deep Pipeline of Programs for Lysosomal Storage Disorders

M6P Therapeutics, a privately held life sciences company developing next-generation recombinant enzyme and gene therapies for lysosomal storage disorders (LSDs), today announced that the U.S. Food and ...
Nature

Lysosomal ceroid depletion by drugs: Therapeutic implications for a hereditary neurodegenerative disease of childhood

Neuronal ceroid lipofuscinoses (NCLs) are the most common hereditary neurodegenerative diseases of childhood. The infantile form, INCL, is caused by lysosomal palmitoyl-protein thioesterase (PPT) ...
News Medical

Researchers identify a new gene implicated in rare lysosomal storage disorder

In a rare disease called mucolipidosis type II, people’s hearts and abdomens swell, and their bones grow malformed. A lysosomal storage disorder, mucolipidosis type II causes edema of the internal ...