The first and only approved achondroplasia therapy to provide continuous systemic exposure to CNP over the weekly dosing ...

Feb 27 (Reuters) - The U.S. Food and Drug Administration on Friday approved Ascendis Pharma's once-weekly therapy for children with a rare genetic disorder that causes dwarfism, the company said. The ...

Achondroplasia, also known as short-limb dwarfism, is associated with neurological symptoms and complications due to narrowing of the skeletal structures surrounding the spinal cord.

Add Yahoo as a preferred source to see more of our stories on Google. Mackenzie Trush has Spondyloepimetaphyseal dysplasia (SEMD), a rare form of dwarfism with less than 100 known cases. Trush is 36 ...

Feb 12 (Reuters) - BridgeBio Pharma said its experimental therapy boosted growth rates in children with a rare genetic disorder that causes dwarfism, sending the company's shares 7% higher on Thursday ...

Add Yahoo as a preferred source to see more of our stories on Google. “From how I’ve always understood it … [there] are different types of dwarfism,” she began. “Some are dominant genes, and some are ...

Peter Dinklage is most famous for his role as Tyrion Lannister from the series Game of Thrones. However, the popular actor has achondroplasia, a rare genetic form of dwarfism, about which he ...

"People like me are endangered and now they want to make me extinct," Little People of America spokeswoman Leah Smith said in 2015 of the growth drug vosoritide. Getty Images for MAKERS A new drug ...

Shares in BridgeBio were ticking up today after it revealed data from its phase 3 trial of infigratinib in achondroplasia, ...

The pet's owner said he "loves jumping around and playing with his ball and squeaky toys" Ranger, a German shepherd, may look like a puppy, but he’s actually two years old! The pooch, owned by Phoenix ...